Clinical trial
A Phase 1 Study to Evaluate the Safety, Tolerability, and Pharmacokinetics of Intravenously Administered PYC-003, a Peptide-phosphorodiamidate Morpholino Oligonucleotide Conjugate, in Healthy Adult Participants and Adult Participants With Confirmed PKD1 Mutation-associated Autosomal Dominant Polycystic Kidney Disease
NCT06714006 is registered in ClinicalTrials.gov with PYC Therapeutics as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- A Phase 1 Study to Evaluate the Safety, Tolerability, and Pharmacokinetics of Intravenously Administered PYC-003, a Peptide-phosphorodiamidate Morpholino Oligonucleotide Conjugate, in Healthy Adult Participants and Adult Participants With Confirmed PKD1 Mutation-associated Autosomal Dominant Polycystic Kidney Disease
- Lead sponsor
- PYC Therapeutics
- Phase
- Phase 1
- Overall status
- Recruiting
- Start date
- April 7, 2025
- Completion date
- November 30, 2028
- Enrollment
- 166 (estimated)
- Sites
- 12
Conditions
As the registry lists them; a condition with its own page is linked.
autosomal dominant polycystic kidney disease (adpkd)