Clinical trial
An Off-Label Single Arm Clinical Study to Evaluate the Efficacy and Safety of Doxecitin and Doxribthymine in Adult Subjects With Thymidine Kinase 2 (TK2) Deficiency.
NCT06754098 is registered in ClinicalTrials.gov with Cristina Domínguez González as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- An Off-Label Single Arm Clinical Study to Evaluate the Efficacy and Safety of Doxecitin and Doxribthymine in Adult Subjects With Thymidine Kinase 2 (TK2) Deficiency.
- Lead sponsor
- Cristina Domínguez González
- Phase
- Phase 2
- Overall status
- Recruiting
- Start date
- January 1, 2025
- Completion date
- December 31, 2027
- Enrollment
- 15 (estimated)
- Sites
- 1
Conditions
As the registry lists them; a condition with its own page is linked.
mitochondrial myopathies, thymidine kinase 2 (tk2 ) deficiency