Clinical trial
A Multi-center, Ambispective Cohort Study to Evaluate the Impact of Iptacopan on Disease Management, Treatment-Related Outcomes and Healthcare Resource Utilization for Adult Patients With Paroxysmal Nocturnal Hemoglobinuria in China
NCT06931691 is registered in ClinicalTrials.gov with Novartis Pharmaceuticals as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- A Multi-center, Ambispective Cohort Study to Evaluate the Impact of Iptacopan on Disease Management, Treatment-Related Outcomes and Healthcare Resource Utilization for Adult Patients With Paroxysmal Nocturnal Hemoglobinuria in China
- Lead sponsor
- Novartis Pharmaceuticals
- Phase
- Observational
- Overall status
- Recruiting
- Start date
- June 10, 2025
- Completion date
- April 21, 2027
- Enrollment
- 80 (estimated)
- Sites
- 14
Conditions
As the registry lists them; a condition with its own page is linked.
paroxysmal nocturnal hemoglobinuria