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Clinical trial

An Individual Patient, Open Label Study to Use ACER-001 to Treat Combined D,L-2-hydroxyglutaric Aciduria (C-2HGA)

NCT07125066 is registered in ClinicalTrials.gov with Jerry Vockley, MD, PhD as lead sponsor.

NCT NCT07125066
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Registry record

As filed in ClinicalTrials.gov.

Title
An Individual Patient, Open Label Study to Use ACER-001 to Treat Combined D,L-2-hydroxyglutaric Aciduria (C-2HGA)
Lead sponsor
Jerry Vockley, MD, PhD
Phase
Phase 1
Overall status
Enrolling by invitation
Start date
July 30, 2025
Completion date
December 31, 2027
Enrollment
1 (estimated)
Sites
1

Conditions

As the registry lists them; a condition with its own page is linked.

combined d,l-2-hydroxyglutaric aciduria