Clinical trial
A Clinical Exploration Study of Adeno-Associated Virus Vector Expressing Human Phenylalanine Hydroxylase Gene in Adult Classical Phenylketonuria
NCT07318909 is registered in ClinicalTrials.gov with Gritgen Therapeutics Co., Ltd. as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- A Clinical Exploration Study of Adeno-Associated Virus Vector Expressing Human Phenylalanine Hydroxylase Gene in Adult Classical Phenylketonuria
- Lead sponsor
- Gritgen Therapeutics Co., Ltd.
- Phase
- Phase 1
- Overall status
- Not yet recruiting
- Start date
- December 31, 2027
- Completion date
- December 31, 2032
- Enrollment
- 9 (estimated)
- Sites
- 1
Conditions
As the registry lists them; a condition with its own page is linked.
phenylketonuria (pku)