Clinical trial
A Prospective, Single-center, Open-label, Single-arm Clinical Study to Evaluate the Safety and Efficacy of CS-121, an In Vivo Base Editing Therapy Delivered by Lipid Nanoparticles Targeting APOC3, in Children and Adolescents With Hyperchylomicronemia
NCT07371767 is registered in ClinicalTrials.gov with Shanghai Jiao Tong University School of Medicine as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- A Prospective, Single-center, Open-label, Single-arm Clinical Study to Evaluate the Safety and Efficacy of CS-121, an In Vivo Base Editing Therapy Delivered by Lipid Nanoparticles Targeting APOC3, in Children and Adolescents With Hyperchylomicronemia
- Lead sponsor
- Shanghai Jiao Tong University School of Medicine
- Phase
- Phase 1
- Overall status
- Recruiting
- Start date
- January 26, 2026
- Completion date
- January 31, 2041
- Enrollment
- 15 (estimated)
- Sites
- 1
Conditions
As the registry lists them; a condition with its own page is linked.
hyperchylomicronemia