Clinical trial
Phase 1/2b Gene Transfer Clinical Trial for Variant Late Infantile Neuronal Ceroid Lipofuscinosis (CLN6 Batten Disease), Delivering the CLN6 Gene by Self-Complementary AAV9
NCT07582484 is registered in ClinicalTrials.gov with The Charlotte and Gwenyth Gray Foundation as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- Phase 1/2b Gene Transfer Clinical Trial for Variant Late Infantile Neuronal Ceroid Lipofuscinosis (CLN6 Batten Disease), Delivering the CLN6 Gene by Self-Complementary AAV9
- Lead sponsor
- The Charlotte and Gwenyth Gray Foundation
- Phase
- Phase 1/2
- Overall status
- Not yet recruiting
- Start date
- August 31, 2026
- Completion date
- August 31, 2028
- Enrollment
- 12 (estimated)
- Sites
- 1
Conditions
As the registry lists them; a condition with its own page is linked.
batten disease, batten's disease, cln6, neuronal ceroid lipofuscinosis, neuronal ceroid lipofuscinosis cln6