Clinical trial
An Open Label, Single Center, Exploratory Study of the Safety and Efficacy of Avalglucosidase Alfa Patients With Non-classic Pompe Disease Aged ≥ 5 Years
NCT07652814 is registered in ClinicalTrials.gov with Iris Plug as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- An Open Label, Single Center, Exploratory Study of the Safety and Efficacy of Avalglucosidase Alfa Patients With Non-classic Pompe Disease Aged ≥ 5 Years
- Lead sponsor
- Iris Plug
- Phase
- Phase 4
- Overall status
- Active, not recruiting
- Start date
- October 13, 2022
- Completion date
- March 9, 2028
- Enrollment
- 6 (estimated)
- Sites
- 1
Conditions
As the registry lists them; a condition with its own page is linked.
glycogen storage disease type ii late onset, pompe disease, pompe disease (late-onset), pompe disease late-onset, pompe's disease juvenile onset