Skip to content
Pharma Observatory a Scientist.com platform

Clinical trial

An Open-label Study of an Experimental Antisense Oligonucleotide Treatment for Amyotrophic Lateral Sclerosis (ALS) Due to TARDBP (TDP-43) Genetic Mutation

NCT07743268 is registered in ClinicalTrials.gov with n-Lorem Foundation as lead sponsor.

NCT NCT07743268
Email me this page as a PDF

Search trials, sites, companies and investigators, and follow each one to the others. Individual plan, $249/seat/mo. Card required.

Get the NCT07743268 report as a PDF

The PDF carries up to 50 rows of each section, where the page shows the first few, with the sources listed. Enter a work email and confirm it from the message we send, and the report follows by email.

Registry record

As filed in ClinicalTrials.gov.

Title
An Open-label Study of an Experimental Antisense Oligonucleotide Treatment for Amyotrophic Lateral Sclerosis (ALS) Due to TARDBP (TDP-43) Genetic Mutation
Lead sponsor
n-Lorem Foundation
Phase
Phase 1/2
Overall status
Enrolling by invitation
Start date
February 19, 2026
Completion date
February 29, 2028
Enrollment
6 (estimated)
Sites
2

Conditions

As the registry lists them; a condition with its own page is linked.

amyotrophic lateral sclerosis (als)