Condition (MeSH)
Lafora Disease
ClinicalTrials.gov lists 4 trials for Lafora Disease or a narrower condition beneath it.
Search trials, drugs, companies and investigators, and follow each one to the others. Individual plan, $249/seat/mo. Card required.
Trials per phase
4 of the 4 trials are tagged with Lafora Disease itself; the rest are tagged with a narrower condition beneath it.
When did Lafora Disease trials start? (3)
Shown in this order: most recent first, 1990 onwards. 2026 is partial: trials registered with a 2026 start date so far, not a full year.
Trials over time, by phase
- Phase 1/2
- Observational
Top of scale: 1
Trials registered with a start date in each year, 1990 onward, stacked by phase (complete years only; the current partial year is in the table's notes). The table below lists the same counts, most recent years first.
| Year | Trials started |
|---|---|
| 2024 | 1 |
| 2019 | 1 |
| 2000 | 1 |
No forecast is made for this condition: it averages 0.2 trial starts a year over the five years to September, under the 5 a year the method needs.
Recruitment duration, a model prediction: 1 trial still running at the 2026-10-09 snapshot, fewer than the 5 needed for a median. Source: ClinicalTrials.gov / AACT (CTTI), public domain.
What phase are Lafora Disease trials in? (3)
Shown in this order: phase order.
Show the trials by phase as a table
| Phase | Trials |
|---|---|
| Phase 1/2 | 1 |
| Observational | 2 |
| Expanded access | 1 |
How many Lafora Disease trials are recruiting? (3)
Shown in this order: the order a trial moves through, from not yet recruiting to unknown.
| Status | Trials |
|---|---|
| Recruiting | 1 |
| Available | 1 |
| Completed | 2 |
Status as registered on ClinicalTrials.gov. Each trial is counted once.
Which lead sponsors run the most Lafora Disease trials? (3)
Shown in this order: most trials first. Lead sponsors the registry classes as industry, NIH, US federal, other government or network. A hospital or university the registry files as government can appear here. Sponsors it classes as academic or other are shown on the full page, because that class cannot separate an institution from a named investigator.
| Sponsor | Trials |
|---|---|
| Ionis Pharmaceuticals, Inc. | 1 |
| National Institute of Neurological Disorders and Stroke (NINDS) | 1 |
| Parasail, LLC | 1 |
Which publications cover Lafora Disease? (1)
Shown in this order: major-topic papers first, then newest, then most linked to trials.
| Publication | Journal | Year | Major topic |
|---|---|---|---|
| Oxidative stress in developmental brain disorders. | Neuropathology : official journal of the Japanese Society of Neuropathology | 2009 | No |
Prevalence (12)
Shown in this order: jurisdiction, then disease name. Orphanet observation for the mapped ORPHA concept; the mapping relation column says whether that concept is exactly this condition or broader or narrower.
| Orphanet disease | Type | Class | Geography | Jurisdiction | Mapping relation |
|---|---|---|---|---|---|
| Lafora disease | Point prevalence | 1-9 / 1 000 000 | Worldwide | Not stated | Exact |
| Lafora disease | Point prevalence | 1-9 / 1 000 000 | France | Not stated | Exact |
| Lafora disease | Cases families | Worldwide | Not stated | Unspecified | |
| Lafora disease | Point prevalence | 1-9 / 1 000 000 | Europe | Not stated | Unspecified |
| Lafora disease | Point prevalence | 1-9 / 1 000 000 | Worldwide | Not stated | Exact |
Showing 5 of 12 prevalence observations.
Rare-disease identity (2)
Shown in this order: exact, broader, narrower, other.
| Orphanet disease | ORPHA code | Relation | Source |
|---|---|---|---|
| Lafora disease | 501 | Exact | Orphanet Rare Disease Ontology (ORDO) |
| Lafora disease | 501 | Exact | Orphadata Science knowledge files, Product 1 |
Not on this page
Not measured: delivery record.
Checked, with nothing recorded for this condition: serious adverse events in this condition's trials and sub-conditions in mesh.
Not computed for conditions with fewer than 10 trials: drugs tested.