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Condition (MeSH)

Donohue Syndrome

ClinicalTrials.gov lists 1 trial for Donohue Syndrome or a narrower condition beneath it. National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) has the most among industry and government lead sponsors, with 1.

MeSH D056731 Musculoskeletal Diseases C05 C16 C18 C19 Listed by Orphanet as a rare disease
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Trials started per year Trials started per year 1 Trials by phase Trials by phase 1 Trials by recruitment status Trials by recruitment status 1 Lead sponsors Lead sponsors 1 Publications Publications 2 Prevalence Prevalence 9 Rare-disease identity Rare-disease identity 2 Trials started per year Trials started per year 1 Trials by phase Trials by phase 1 Trials by recruitment status Trials by recruitment status 1 Lead sponsors Lead sponsors 1 Publications Publications 2 Prevalence Prevalence 9 Rare-disease identity Rare-disease identity 2

Rows recorded per section

2 sections measured, none recorded · 1 not measured yet · 1 not computed

1 of the 1 trial is tagged with Donohue Syndrome itself; the rest are tagged with a narrower condition beneath it.

Get the Donohue Syndrome report as a PDF

The PDF carries up to 50 rows of each section, where the page shows the first few, with the sources listed. Enter a work email and confirm it from the message we send, and the report follows by email.

When did Donohue Syndrome trials start? (1)

Shown in this order: most recent first, 1990 onwards. 2026 is partial: trials registered with a 2026 start date so far, not a full year.

Trials started per year
Year Trials started
2001 1

No forecast is made for this condition: it averages 0.0 trial starts a year over the five years to September, under the 5 a year the method needs.

Recruitment duration, a model prediction: none of the 1 trial evaluated at the 2026-10-09 snapshot is predicted and still running. Source: ClinicalTrials.gov / AACT (CTTI), public domain.

What phase are Donohue Syndrome trials in? (1)

Shown in this order: phase order.

Trials by phase
Phase Trials
Phase 2 1

How many Donohue Syndrome trials are recruiting? (1)

Shown in this order: the order a trial moves through, from not yet recruiting to unknown.

Trials by recruitment status
Status Trials
Completed 1

Status as registered on ClinicalTrials.gov. Each trial is counted once.

Which lead sponsors run the most Donohue Syndrome trials? (1)

Shown in this order: most trials first. Lead sponsors the registry classes as industry, NIH, US federal, other government or network. A hospital or university the registry files as government can appear here. Sponsors it classes as academic or other are shown on the full page, because that class cannot separate an institution from a named investigator.

Lead sponsors
Sponsor Trials
National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) 1

Which publications cover Donohue Syndrome? (2)

Shown in this order: major-topic papers first, then newest, then most linked to trials.

Publications
Publication Journal Year Major topic
Long-Term Effects of Metreleptin in Rabson-Mendenhall Syndrome on Glycemia, Growth, and Kidney Function. The Journal of clinical endocrinology and metabolism 2022 Yes
Metreleptin improves blood glucose in patients with insulin receptor mutations. The Journal of clinical endocrinology and metabolism 2013 Yes

Prevalence (9)

Shown in this order: jurisdiction, then disease name. Orphanet observation for the mapped ORPHA concept; the mapping relation column says whether that concept is exactly this condition or broader or narrower.

Prevalence
Orphanet disease Type Class Geography Jurisdiction Mapping relation
Donohue syndrome Point prevalence <1 / 1 000 000 Worldwide Not stated Unspecified
Donohue syndrome Prevalence at birth <1 / 1 000 000 Europe Not stated Exact
Donohue syndrome Point prevalence <1 / 1 000 000 Europe Not stated Exact
Donohue syndrome Prevalence at birth <1 / 1 000 000 Europe Not stated Unspecified
Donohue syndrome Point prevalence <1 / 1 000 000 Worldwide Not stated Exact

Rare-disease identity (2)

Shown in this order: exact, broader, narrower, other.

Rare-disease identity
Orphanet disease ORPHA code Relation Source
Donohue syndrome 508 Exact Orphanet Rare Disease Ontology (ORDO)
Donohue syndrome 508 Exact Orphadata Science knowledge files, Product 1

Not on this page

Not measured: delivery record.

Checked, with nothing recorded for this condition: serious adverse events in this condition's trials and sub-conditions in mesh.

Not computed for conditions with fewer than 10 trials: drugs tested.

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