Clinical trial
Hematopoietic Stem Cell Transplantation for Hurler Syndrome, Maroteaux Lamy Syndrome (MPS VI), and Alpha Mannosidase Deficiency (Mannosidosis)
NCT00176917 is registered in ClinicalTrials.gov with Masonic Cancer Center, University of Minnesota as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- Hematopoietic Stem Cell Transplantation for Hurler Syndrome, Maroteaux Lamy Syndrome (MPS VI), and Alpha Mannosidase Deficiency (Mannosidosis)
- Lead sponsor
- Masonic Cancer Center, University of Minnesota
- Phase
- Phase 2
- Overall status
- Completed
- Start date
- May 31, 1999
- Completion date
- May 31, 2010
- Enrollment
- 41 (actual)
- Sites
- 1
Conditions
As the registry lists them; a condition with its own page is linked.
mannosidosis, mucolipidosis type ii (i-cell disease), mucopolysaccharidosis i, mucopolysaccharidosis vi