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Clinical trial

A Multicenter Study to Evaluate and Characterize the Effects of Pharmacological Chaperones in Cell Lines Derived From Blood and Skin Samples From Patients With Pompe Disease

NCT00515398 is registered in ClinicalTrials.gov with Amicus Therapeutics as lead sponsor.

NCT NCT00515398
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Registry record

As filed in ClinicalTrials.gov.

Title
A Multicenter Study to Evaluate and Characterize the Effects of Pharmacological Chaperones in Cell Lines Derived From Blood and Skin Samples From Patients With Pompe Disease
Lead sponsor
Amicus Therapeutics
Phase
Observational
Overall status
Completed
Start date
August 31, 2007
Completion date
January 31, 2008
Enrollment
30 (actual)
Sites
4

Conditions

As the registry lists them; a condition with its own page is linked.

glycogen storage disease type ii, pompe disease