Clinical trial
A Randomized, Double-Blind, Placebo-Controlled Study to Assess the Safety and Efficacy of Mipomersen as Add-on Therapy in Homozygous Familial Hypercholesterolemia Subjects
NCT00607373 is registered in ClinicalTrials.gov with Kastle Therapeutics, LLC as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- A Randomized, Double-Blind, Placebo-Controlled Study to Assess the Safety and Efficacy of Mipomersen as Add-on Therapy in Homozygous Familial Hypercholesterolemia Subjects
- Lead sponsor
- Kastle Therapeutics, LLC
- Phase
- Phase 3
- Overall status
- Completed
- Start date
- July 31, 2007
- Completion date
- March 31, 2009
- Enrollment
- 51 (actual)
- Sites
- 10
Conditions
As the registry lists them; a condition with its own page is linked.
congenital abnormalities, dyslipidemias, genetic diseases, inborn, hypercholesterolemia, hypercholesterolemia, autosomal dominant, hyperlipidemias, hyperlipoproteinemia type ii, hyperlipoproteinemias, infant, newborn, diseases, lipid metabolism disorders, lipid metabolism, inborn errors, metabolic diseases, metabolic disorder, metabolism, inborn errors