Clinical trial
A Phase I/II Safety, Tolerability, Ascending Dose and Dose Frequency Study of Recombinant Human Heparan N-Sulfatase (rhHNS) Intrathecal Administration Via an Intrathecal Drug Delivery Device in Patients With Sanfilippo Syndrome Type A (MPS IIIA)
NCT01155778 is registered in ClinicalTrials.gov with Shire as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- A Phase I/II Safety, Tolerability, Ascending Dose and Dose Frequency Study of Recombinant Human Heparan N-Sulfatase (rhHNS) Intrathecal Administration Via an Intrathecal Drug Delivery Device in Patients With Sanfilippo Syndrome Type A (MPS IIIA)
- Lead sponsor
- Shire
- Phase
- Phase 1/2
- Overall status
- Completed
- Start date
- June 1, 2010
- Completion date
- September 1, 2012
- Enrollment
- 12 (actual)
- Sites
- 2
Conditions
As the registry lists them; a condition with its own page is linked.
mucopolysaccharidosis (mps)