Skip to content
Pharma Observatory a Scientist.com platform

Clinical trial

The Use of Novel Therapies to Reconstitute Blood Cell Production and Promote Organ Performance Using Bone Marrow Failure as a Model: a Pilot, Phase I/II Study of the Amino Acid Leucine in the Treatment of Patients With Transfusion-Dependent Diamond Blackfan Anemia

NCT01362595 is registered in ClinicalTrials.gov with Northwell Health as lead sponsor.

NCT NCT01362595
Email me this page as a PDF

Search trials, sites, companies and investigators, and follow each one to the others. Individual plan, $249/seat/mo. Card required.

Get the NCT01362595 report as a PDF

The PDF carries up to 50 rows of each section, where the page shows the first few, with the sources listed. Enter a work email and confirm it from the message we send, and the report follows by email.

Registry record

As filed in ClinicalTrials.gov.

Title
The Use of Novel Therapies to Reconstitute Blood Cell Production and Promote Organ Performance Using Bone Marrow Failure as a Model: a Pilot, Phase I/II Study of the Amino Acid Leucine in the Treatment of Patients With Transfusion-Dependent Diamond Blackfan Anemia
Lead sponsor
Northwell Health
Phase
Phase 1/2
Overall status
Completed
Start date
June 30, 2013
Completion date
November 30, 2020
Enrollment
55 (actual)
Sites
11

Conditions

As the registry lists them; a condition with its own page is linked.

blackfan diamond syndrome, congenital hypoplastic anemia, dba, diamond blackfan anemia, pure red cell aplasia