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Clinical trial

Direct CNS Administration of a Replication Deficient Adeno-associated Virus Gene Transfer Vector Serotype rh.10 Expressing the Human CLN2 cDNA to Children With LINCL With Uncommon Genotypes and/or Moderate to Severe Impairment

NCT01414985 is registered in ClinicalTrials.gov with Weill Medical College of Cornell University as lead sponsor.

NCT NCT01414985
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Registry record

As filed in ClinicalTrials.gov.

Title
Direct CNS Administration of a Replication Deficient Adeno-associated Virus Gene Transfer Vector Serotype rh.10 Expressing the Human CLN2 cDNA to Children With LINCL With Uncommon Genotypes and/or Moderate to Severe Impairment
Lead sponsor
Weill Medical College of Cornell University
Phase
Phase 1/2
Overall status
Completed
Start date
April 15, 2010
Completion date
February 8, 2017
Enrollment
8 (actual)
Sites
1

Conditions

As the registry lists them; a condition with its own page is linked.

batten disease, late infantile neuronal ceroid lipofuscinosis