Clinical trial
A Multicenter, Multinational, Extension Study to Evaluate the Long-Term Efficacy and Safety of BMN 190 in Patients With CLN2 Disease
NCT02485899 is registered in ClinicalTrials.gov with BioMarin Pharmaceutical as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- A Multicenter, Multinational, Extension Study to Evaluate the Long-Term Efficacy and Safety of BMN 190 in Patients With CLN2 Disease
- Lead sponsor
- BioMarin Pharmaceutical
- Phase
- Phase 1/2
- Overall status
- Completed
- Start date
- February 28, 2015
- Completion date
- December 10, 2020
- Enrollment
- 23 (actual)
- Sites
- 4
Conditions
As the registry lists them; a condition with its own page is linked.
batten disease, cln2 disease, cln2 disorder, jansky-bielschowsky disease, late-infantile neuronal ceroid lipofuscinosis type 2