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Clinical trial

Open-label, Single-arm, Multi-center Study of Intracerebral Administration of Adeno-associated Viral (AAV) Serotype rh.10 Carrying Human N-sulfoglucosamine Sulfohydrolase (SGSH) cDNA for Treatment of Mucopolysaccharidosis Type IIIA

NCT03612869 is registered in ClinicalTrials.gov with LYSOGENE as lead sponsor.

NCT NCT03612869
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Registry record

As filed in ClinicalTrials.gov.

Title
Open-label, Single-arm, Multi-center Study of Intracerebral Administration of Adeno-associated Viral (AAV) Serotype rh.10 Carrying Human N-sulfoglucosamine Sulfohydrolase (SGSH) cDNA for Treatment of Mucopolysaccharidosis Type IIIA
Lead sponsor
LYSOGENE
Phase
Phase 2/3
Overall status
Unknown status
Start date
December 17, 2018
Completion date
March 31, 2022
Enrollment
20 (estimated)
Sites
8

Conditions

As the registry lists them; a condition with its own page is linked.

mucopolysaccharidosis type iiia