Clinical trial
Long-term Follow-up of Patients With Sanfilippo Type A Syndrome Who Have Previously Been Treated in the P1-SAF-301 Clinical Study Evaluating the Tolerability and Safety of the Intracerebral Administration of SAF-301.
NCT02053064 is registered in ClinicalTrials.gov with LYSOGENE as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- Long-term Follow-up of Patients With Sanfilippo Type A Syndrome Who Have Previously Been Treated in the P1-SAF-301 Clinical Study Evaluating the Tolerability and Safety of the Intracerebral Administration of SAF-301.
- Lead sponsor
- LYSOGENE
- Phase
- Phase 1/2
- Overall status
- Completed
- Start date
- May 31, 2013
- Completion date
- June 30, 2017
- Enrollment
- 4 (actual)
- Sites
- 1
Conditions
As the registry lists them; a condition with its own page is linked.
mucopolysaccharidosis type iii a, sanfilippo disease type a