Clinical trial
Developing a Management Approach for Patients With "Late-Onset" Pompe Disease GAA Variant Identified by Newborn Screening
NCT03694561 is registered in ClinicalTrials.gov with Duke University as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- Developing a Management Approach for Patients With "Late-Onset" Pompe Disease GAA Variant Identified by Newborn Screening
- Lead sponsor
- Duke University
- Phase
- Observational
- Overall status
- Active, not recruiting
- Start date
- March 25, 2019
- Completion date
- August 31, 2027
- Enrollment
- 20 (estimated)
- Sites
- 1
Conditions
As the registry lists them; a condition with its own page is linked.
gaa deficiency, pompe disease, pompe disease (late-onset)