Clinical trial
An Open-Label Study of Risdiplam in Infants With Genetically Diagnosed and Presymptomatic Spinal Muscular Atrophy
NCT03779334 is registered in ClinicalTrials.gov with Hoffmann-La Roche as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- An Open-Label Study of Risdiplam in Infants With Genetically Diagnosed and Presymptomatic Spinal Muscular Atrophy
- Lead sponsor
- Hoffmann-La Roche
- Phase
- Phase 2
- Overall status
- Active, not recruiting
- Start date
- August 7, 2019
- Completion date
- February 28, 2027
- Enrollment
- 26 (actual)
- Sites
- 7
Conditions
As the registry lists them; a condition with its own page is linked.