Clinical trial
An Open, Single-arm, Multicenter Extension Study to Assess the Safety, Tolerability, and Efficacy of Long-term SOBI003 Treatment in Pediatric MPS IIIA Patients
NCT03811028 is registered in ClinicalTrials.gov with Swedish Orphan Biovitrum as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- An Open, Single-arm, Multicenter Extension Study to Assess the Safety, Tolerability, and Efficacy of Long-term SOBI003 Treatment in Pediatric MPS IIIA Patients
- Lead sponsor
- Swedish Orphan Biovitrum
- Phase
- Phase 1/2
- Overall status
- Completed
- Start date
- January 19, 2019
- Completion date
- May 7, 2021
- Enrollment
- 6 (actual)
- Sites
- 3
Conditions
As the registry lists them; a condition with its own page is linked.
sanfilippo syndrome type a (mps iiia)