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Clinical trial

PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)

NCT04532047 is registered in ClinicalTrials.gov with University of California, San Francisco as lead sponsor.

NCT NCT04532047
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Registry record

As filed in ClinicalTrials.gov.

Title
PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)
Lead sponsor
University of California, San Francisco
Phase
Phase 1
Overall status
Recruiting
Start date
July 1, 2021
Completion date
July 31, 2032
Enrollment
10 (estimated)
Sites
1

Conditions

As the registry lists them; a condition with its own page is linked.

gaucher disease, type 2, gaucher disease, type 3, mps i, mps ii, mps iva, mps vi, mps vii, pompe disease infantile-onset, wolman disease