Clinical trial
Eight At One Stroke: Attention Gangliosidoses A Registry Study for Patients With Gangliosidoses
NCT04624789 is registered in ClinicalTrials.gov with SphinCS Lyso Gemeinnutzige UG (Haftungsbeschrankt) as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- Eight At One Stroke: Attention Gangliosidoses A Registry Study for Patients With Gangliosidoses
- Lead sponsor
- SphinCS Lyso Gemeinnutzige UG (Haftungsbeschrankt)
- Phase
- Observational
- Overall status
- Unknown status
- Start date
- June 8, 2020
- Completion date
- June 7, 2025
- Enrollment
- 40 (estimated)
- Sites
- 1
Conditions
As the registry lists them; a condition with its own page is linked.
galactosialidosis, gangliosidoses, gm1 gangliosidosis, gm2 activator deficiency, gm2-gangliosidosis, variant b1, morquio b disease, sandhoff disease, sialidosis, tay-sachs disease