Clinical trial
Clinical, Instrumental and Laboratory Data Collection of Subjects with Ultra-rare Inherited Metabolic and Degenerative Neurological Diseases
NCT04880356 is registered in ClinicalTrials.gov with Fondazione I.R.C.C.S. Istituto Neurologico Carlo Besta as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- Clinical, Instrumental and Laboratory Data Collection of Subjects with Ultra-rare Inherited Metabolic and Degenerative Neurological Diseases
- Lead sponsor
- Fondazione I.R.C.C.S. Istituto Neurologico Carlo Besta
- Phase
- Observational
- Overall status
- Recruiting
- Start date
- March 1, 2021
- Completion date
- March 31, 2031
- Enrollment
- 100 (estimated)
- Sites
- 1
Conditions
As the registry lists them; a condition with its own page is linked.
inherited disease, metabolic disease, neuro-degenerative disease, neurologic disorder, rare diseases, undiagnosed disease