Clinical trial
Validation of Therapeutic Efficacy Targeting the Splicing Variants in Cystic Fibrosis and CFTR Pathologies
NCT05100823 is registered in ClinicalTrials.gov with University Hospital, Montpellier as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- Validation of Therapeutic Efficacy Targeting the Splicing Variants in Cystic Fibrosis and CFTR Pathologies
- Lead sponsor
- University Hospital, Montpellier
- Phase
- Not applicable
- Overall status
- Terminated
- Start date
- March 30, 2022
- Completion date
- February 17, 2025
- Enrollment
- 16 (actual)
- Sites
- 1
Conditions
As the registry lists them; a condition with its own page is linked.
cftr gene mutation, cystic fibrosis