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Clinical trial

An Open-Label Study to Evaluate Pharmacokinetics, Safety, and Efficacy of Vatiquinone in Children With Friedreich Ataxia Younger Than 7 Years of Age

NCT05485987 is registered in ClinicalTrials.gov with PTC Therapeutics as lead sponsor.

NCT NCT05485987
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Registry record

As filed in ClinicalTrials.gov.

Title
An Open-Label Study to Evaluate Pharmacokinetics, Safety, and Efficacy of Vatiquinone in Children With Friedreich Ataxia Younger Than 7 Years of Age
Lead sponsor
PTC Therapeutics
Phase
Phase 2
Overall status
Completed
Start date
October 12, 2022
Completion date
August 29, 2024
Enrollment
5 (actual)
Sites
1

Conditions

As the registry lists them; a condition with its own page is linked.

friedreich ataxia