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Clinical trial

Open-Label Multicenter Extension Study to Further Evaluate Safety, Tolerability and Efficacy of Intracerebroventricular AX 250 Treatment in Mucopolysaccharidosis Type IIIB (MPS IIIB, Sanfilippo Syndrome Type B) Patients

NCT05492799 is registered in ClinicalTrials.gov with Allievex Corporation as lead sponsor.

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Registry record

As filed in ClinicalTrials.gov.

Title
Open-Label Multicenter Extension Study to Further Evaluate Safety, Tolerability and Efficacy of Intracerebroventricular AX 250 Treatment in Mucopolysaccharidosis Type IIIB (MPS IIIB, Sanfilippo Syndrome Type B) Patients
Lead sponsor
Allievex Corporation
Phase
Phase 4
Overall status
Enrolling by invitation
Start date
December 2, 2022
Completion date
December 31, 2027
Enrollment
15 (estimated)
Sites
6

Conditions

As the registry lists them; a condition with its own page is linked.

mps iii b