Clinical trial
A Phase 1/2 Open-Label Dose-Escalation Study to Evaluate the Safety, Tolerability, Pharmacokinetics and Efficacy of Intracerebroventricular AX 250 in Patients With Mucopolysaccharidosis Type IIIB (MPS IIIB, Sanfilippo Syndrome Type B)
NCT02754076 is registered in ClinicalTrials.gov with Allievex Corporation as lead sponsor.
Search trials, sites, companies and investigators, and follow each one to the others. Individual plan, $249/seat/mo. Card required.
Registry record
As filed in ClinicalTrials.gov.
- Title
- A Phase 1/2 Open-Label Dose-Escalation Study to Evaluate the Safety, Tolerability, Pharmacokinetics and Efficacy of Intracerebroventricular AX 250 in Patients With Mucopolysaccharidosis Type IIIB (MPS IIIB, Sanfilippo Syndrome Type B)
- Lead sponsor
- Allievex Corporation
- Phase
- Phase 1/2
- Overall status
- Completed
- Start date
- April 30, 2016
- Completion date
- July 31, 2020
- Enrollment
- 23 (actual)
- Sites
- 7
Conditions
As the registry lists them; a condition with its own page is linked.
mps iii b, mucopolysaccharidosis type iiib