Clinical trial
Randomized, Double Blind, Placebo Controlled, Multicenter, 12 Weeks Phase 2 Study to Evaluate the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of Oral AZ-3102 in Patients With GM2 Gangliosidosis or Niemann-Pick Type C Disease
NCT05758922 is registered in ClinicalTrials.gov with Azafaros B.V. as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- Randomized, Double Blind, Placebo Controlled, Multicenter, 12 Weeks Phase 2 Study to Evaluate the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of Oral AZ-3102 in Patients With GM2 Gangliosidosis or Niemann-Pick Type C Disease
- Lead sponsor
- Azafaros B.V.
- Phase
- Phase 2
- Overall status
- Completed
- Start date
- April 24, 2023
- Completion date
- May 5, 2026
- Enrollment
- 13 (actual)
- Sites
- 3
Conditions
As the registry lists them; a condition with its own page is linked.
gm2 gangliosidosis, niemann-pick disease, type c