Clinical trial
A Long-Term Follow-Up Study in Subjects With Severe Hemophilia A Who Received BMN 270, an Adeno-Associated Virus Vector-Mediated Gene Transfer of Human Factor VIII in a Prior BioMarin Clinical Trial
NCT05768386 is registered in ClinicalTrials.gov with BioMarin Pharmaceutical as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- A Long-Term Follow-Up Study in Subjects With Severe Hemophilia A Who Received BMN 270, an Adeno-Associated Virus Vector-Mediated Gene Transfer of Human Factor VIII in a Prior BioMarin Clinical Trial
- Lead sponsor
- BioMarin Pharmaceutical
- Phase
- Observational
- Overall status
- Enrolling by invitation
- Start date
- January 1, 2023
- Completion date
- January 31, 2040
- Enrollment
- 172 (estimated)
- Sites
- 41
Conditions
As the registry lists them; a condition with its own page is linked.