Clinical trial
A Multicenter, Open-label, Single-dose, Systemic Gene Transfer Study to Evaluate the Safety, Tolerability, and Efficacy of SRP-9003 on Subjects With Limb Girdle Muscular Dystrophy, Type 2E/R4 (β-Sarcoglycan Deficiency)
NCT05876780 is registered in ClinicalTrials.gov with Sarepta Therapeutics, Inc. as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- A Multicenter, Open-label, Single-dose, Systemic Gene Transfer Study to Evaluate the Safety, Tolerability, and Efficacy of SRP-9003 on Subjects With Limb Girdle Muscular Dystrophy, Type 2E/R4 (β-Sarcoglycan Deficiency)
- Lead sponsor
- Sarepta Therapeutics, Inc.
- Phase
- Phase 1
- Overall status
- Active, not recruiting
- Start date
- December 19, 2022
- Completion date
- August 28, 2028
- Enrollment
- 6 (actual)
- Sites
- 2
Conditions
As the registry lists them; a condition with its own page is linked.
limb girdle muscular dystrophy