Clinical trial
A Phase 1b, Multicenter, Single Dose Gene Transfer Study to Evaluate the Safety, Tolerability, and Efficacy of SRP-9004 Administered by Systemic Infusion in Limb Girdle Muscular Dystrophy Type 2D/R3 Subjects in the United States
NCT06747273 is registered in ClinicalTrials.gov with Sarepta Therapeutics, Inc. as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- A Phase 1b, Multicenter, Single Dose Gene Transfer Study to Evaluate the Safety, Tolerability, and Efficacy of SRP-9004 Administered by Systemic Infusion in Limb Girdle Muscular Dystrophy Type 2D/R3 Subjects in the United States
- Lead sponsor
- Sarepta Therapeutics, Inc.
- Phase
- Phase 1
- Overall status
- Terminated
- Start date
- January 9, 2025
- Completion date
- June 18, 2025
- Enrollment
- 4 (actual)
- Sites
- 2
Conditions
As the registry lists them; a condition with its own page is linked.
limb girdle muscular dystrophy, limb girdle muscular dystrophy type 2d/r3