Clinical trial
An Open-Label Single Center, Single Participant Study of an Experimental Antisense Oligonucleotide Treatment for Bainbridge-Ropers Syndrome Due to ASXL3 Gene Variant
NCT07197268 is registered in ClinicalTrials.gov with n-Lorem Foundation as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- An Open-Label Single Center, Single Participant Study of an Experimental Antisense Oligonucleotide Treatment for Bainbridge-Ropers Syndrome Due to ASXL3 Gene Variant
- Lead sponsor
- n-Lorem Foundation
- Phase
- Phase 1/2
- Overall status
- Active, not recruiting
- Start date
- May 19, 2025
- Completion date
- May 31, 2027
- Enrollment
- 1 (actual)
- Sites
- 1
Conditions
As the registry lists them; a condition with its own page is linked.
bainbridge-ropers syndrome