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Clinical trial

Phase 1 Study of Intravenous Administration of a Serotype rh.10 Replication Deficient Adeno-associated Virus Gene Transfer Vector Expressing the Human Propionyl-CoA Carboxylase cDNA (AAVrh10-PCCA) to Individuals With Propionic Acidemia

NCT07643844 is registered in ClinicalTrials.gov with Mayo Clinic as lead sponsor.

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Registry record

As filed in ClinicalTrials.gov.

Title
Phase 1 Study of Intravenous Administration of a Serotype rh.10 Replication Deficient Adeno-associated Virus Gene Transfer Vector Expressing the Human Propionyl-CoA Carboxylase cDNA (AAVrh10-PCCA) to Individuals With Propionic Acidemia
Lead sponsor
Mayo Clinic
Phase
Phase 1
Overall status
Recruiting
Start date
July 20, 2026
Completion date
December 31, 2033
Enrollment
9 (estimated)
Sites
1

Conditions

As the registry lists them; a condition with its own page is linked.