Clinical trial
Potenziare la Gestione Clinica Delle CMF Attraverso Una Rete Nazionale Pediatrica e Dell'Adulto Basata su Dati Biologici e Genetici / Enhancing the Clinical Management of CMF Through a National Pediatric and Adult Network Based on Biological and Genetic Data
NCT07877727 is registered in ClinicalTrials.gov with Istituto Giannina Gaslini as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- Potenziare la Gestione Clinica Delle CMF Attraverso Una Rete Nazionale Pediatrica e Dell'Adulto Basata su Dati Biologici e Genetici / Enhancing the Clinical Management of CMF Through a National Pediatric and Adult Network Based on Biological and Genetic Data
- Lead sponsor
- Istituto Giannina Gaslini
- Phase
- Observational
- Overall status
- Recruiting
- Start date
- May 29, 2025
- Completion date
- December 31, 2026
- Enrollment
- 250 (estimated)
- Sites
- 4
Conditions
As the registry lists them; a condition with its own page is linked.
acquired aplastic anemia, congenital amegakaryocytic thrombocytopenia, congenital neutropenia, dyskeratosis congenita, fanconi anemia, inherited bone marrow failure syndrome, paroxysmal nocturnal hemoglobinuria, pnh, primary immune regulatory disorder, telomere biology disorder