Clinical trial
Natural History Study of Children With Metachromatic Leukodystrophy
NCT01963650 is registered in ClinicalTrials.gov with Shire as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- Natural History Study of Children With Metachromatic Leukodystrophy
- Lead sponsor
- Shire
- Phase
- Observational
- Overall status
- Terminated
- Start date
- November 2, 2015
- Completion date
- April 8, 2016
- Enrollment
- 1 (actual)
- Sites
- 14
Conditions
As the registry lists them; a condition with its own page is linked.
brain diseases, central nervous system diseases, demyelinating diseases, genetic diseases, inborn, hereditary central nervous system demyelinating diseases, lipid metabolism disorders, lysosomal storage diseases, metabolic diseases, metabolic inborn brain diseases, metabolism, inborn errors, metachromatic leukodystrophy (mld), nervous system diseases, sphingolipidoses, sulfatidosis