Clinical trial
An Open-Label, Extension Study to Evaluate the Safety, Tolerability, Efficacy and Pharmacokinetics of QR-110 in Subjects With Leber's Congenital Amaurosis (LCA) Due to the c.2991+1655A>G Mutation (p.Cys998X) in the CEP290 Gene
NCT03913130 is registered in ClinicalTrials.gov with Laboratoires Thea as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- An Open-Label, Extension Study to Evaluate the Safety, Tolerability, Efficacy and Pharmacokinetics of QR-110 in Subjects With Leber's Congenital Amaurosis (LCA) Due to the c.2991+1655A>G Mutation (p.Cys998X) in the CEP290 Gene
- Lead sponsor
- Laboratoires Thea
- Phase
- Phase 1/2
- Overall status
- Terminated
- Start date
- May 13, 2019
- Completion date
- October 3, 2022
- Enrollment
- 9 (actual)
- Sites
- 3
Conditions
As the registry lists them; a condition with its own page is linked.
blindness, eye diseases, eye diseases, hereditary, eye disorders congenital, leber congenital amaurosis, leber congenital amaurosis 10, neurologic manifestations, retinal disease, sensation disorders, vision disorders