Clinical trial
Natural History Study of Infantile and Juvenile GM1 Gangliosidosis (GM1) Patients
NCT04041102 is registered in ClinicalTrials.gov with University of Pennsylvania as lead sponsor.
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Registry record
As filed in ClinicalTrials.gov.
- Title
- Natural History Study of Infantile and Juvenile GM1 Gangliosidosis (GM1) Patients
- Lead sponsor
- University of Pennsylvania
- Phase
- Observational
- Overall status
- Completed
- Start date
- June 12, 2020
- Completion date
- May 1, 2024
- Enrollment
- 31 (actual)
- Sites
- 6
Conditions
As the registry lists them; a condition with its own page is linked.
gm1 gangliosidosis